Search Results for “Case study - research” - Page 7

Four people sitting in a line. The person furthest away from the camera is the only one facing towards it. He is wearing a white shirt

Involving our community

Our community is informed and knowledgeable about current research projects into the cause(s) of and treatments for these conditions.

A high power image showing the position of a single transplanted photoreceptor cell (green) making new connections with bipolar cells in the recipient retina (cyan).

Stem cells are a special type of cell, which under the right conditions can be encouraged to grow into any other type of cell in the body, including retinal cells (rods, cones and retinal pigment epithelial cells).

Learning from your experiences

Thank you to all those who completed our recent Sight Loss Survey – almost 700 of you took the time to share your experiences.

News

Disappointing news from ProQR clinical trial for LCA10

ProQR has published the top-line results from its Phase 2/3 “Illuminate” trial of the RNA therapy sepofarsen for Leber congenital amaurosis type 10 caused by a specific mutation in the CEP290 gene.

Phase 3 clinical trial has been given approval by FDA

The FDA has given Ocugen permission to start their phase 3 gene therapy clinical trial for retinitis pigmentosa (RP).

Drugs for cancer and alcoholism show promise for RP

With all the interest in exciting gene and cell therapies for inherited sight loss, it’s easy to forget that more traditional drugs can also hold promise.

News

Sepul Bio begins clinical trial of ultevursen for USH2A-associated RP

Look Forward – Summer 2023 – Issue 180

Did you join either of our Conferences this year? You can read about them inside this edition of Look Forward. We’ve had some fantastic feedback from our delegates so if you weren’t able to attend, you can watch or listen to the recordings from the day on our website.

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